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Ex Vivo Gene-editing Platform for Hematopoietic Stem Cells
The platform focuses on developing innovative therapies for β-thalassemia and other anemias based on the autologous hematopoietic stem cells through gene editing.
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Ex Vivo Gene-editing Platforms for T Cells
The platform develops the allogeneic CAR-T therapies for cancer, that is to remove receptors and proteins that can cause adverse reactions such as GvH and HvG on T cells of a healthy donor.
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In Vivo Therapeutic Platform Based on RNA Base Editing
The platform develops therapeutics for ophthalmic diseases, neuromuscular diseases, and other genetic/non-genetic diseases based on the RNA base editing technology LEAPER™.
