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Efficient and safe RNA editing in Non-Human Primates using AAV delivered LEAPER agents
May 2023, 26th ASGCT Annual Meeting, Oral Presentation
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Preliminary Safety and Efficacy Results of EDI001: An Investigator Initiated Trial on CRISPR/Cas9-Modified Autologous CD34+ Hematopoietic Stem and Progenitor Cells for Patients with Transfusion Dependent β-Thalassemia
December 2022, 64th ASH Annual Meeting, Poster Presentation
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Quality of Life in Children with Beta-Thalassemia Major: A Cross-Sectional Study in China
June 2022, EHA2022, Poster presentation
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getools Enables Ultra-Fast and Accurate Quantification of Gene-Editing Outcomes with Both Bulk and Single-cell Data from Genome Editing Experiments
May 2022, 25th ASGCT Annual Meeting, Poster Presentation
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Microtubule Polymerization Inhibition Enhances Human Hematopoietic Stem Cell Homing and Engraftment
December 2021, 63rd ASH Annual Meeting, Poster Presentation
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CD66e Enrichment Enhances Repopulation of Human Long-Term Hematopoietic Stem Cells
December 2021, 63 st ASH Annual Meeting, Poster Presentation
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Highly Efficient Gene Editing of Human Hematopoietic Stem Cells to Treat X-Linked Sideroblastic Anemia
December 2020, 62 st ASH Annual Meeting, Poster Presentation
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A Novel Oligonucleotide-Based RNA Base Editing Therapeutic Approach for the Treatment of Hurler Syndrome
May 2020, 23rd ASGCT Annual Meeting, Oral Presentation
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Manufacturing Scale-up and Preclinical Development of ET-01, Autologous CD34+ Cells with the BCL11A Erythroid Enhancer Edited By CRISPR/Cas9, for Patients with β-Thalassemia Major
December 2019, 61st ASH Annual Meeting, Poster Presentation
